R&D Pipeline · RECORNA

Accelerating Novel Therapies
for Unmet Needs

Development Progress

CNS-Targeted Therapies
Population
Indication
Mechanism
DiscoveryPreclinicalIITClinical
Dravet Syndrome / SCN1A
mRNA upregulation
Discovery Preclinical IIT Clinical
Neurodegenerative Diseases
Introduce a protective mutation
Discovery Preclinical IIT Clinical
Liver-Targeted Therapies
Population
Indication
Mechanism
DiscoveryPreclinicalIITClinical
Rare Metabolic Diseases
repair a pathogenic vatiant
Discovery Preclinical IIT Clinical
Metabolic Disorders
repair a pathogenic vatiant
Discovery Preclinical IIT Clinical
Cardiovascular Diseases
mRNA Upregulation
Discovery Preclinical IIT Clinical
Anti-Aging Research
Introduce a beneficial mutation
Discovery Preclinical IIT Clinical